Paediatrics
Paediatrics

Mobility and Quality of Life in Children with Paediatric-Onset Hypophosphatasia Treated with Asfotase Alfa: Results from UK Managed Access Agreement

Adv Ther. 2025 May 29. doi: 10.1007/s12325-025-03225-4. Online ahead of print. ABSTRACT INTRODUCTION: Hypophosphatasia (HPP) is a rare, inherited metabolic bone disease with a high …

Gene Expression Analysis of (Paired) Primary and Relapsed Wilms Tumor Samples to Unravel the Underlying Factors Driving Tumor Recurrence

Cancer Med. 2025 Jun;14(11):e70969. doi: 10.1002/cam4.70969. ABSTRACT PURPOSE: We aimed to unravel underlying factors driving Wilms tumor (WT) recurrence and to build a prediction model …

Ethnicity modifies the association between microRNA single nucleotide polymorphisms and pediatric acute lymphoblastic leukemia risk: a meta-analysis

Biomark Med. 2025 May 29:1-15. doi: 10.1080/17520363.2025.2511466. Online ahead of print. ABSTRACT INTRODUCTION: MicroRNA (miRNA) single nucleotide polymorphisms (miRNA-SNPs) have been associated with pediatric acute …

Towards graft-versus-host disease-free alternative donor transplant platforms for patients with acquired aplastic anemia

Haematologica. 2025 May 29. doi: 10.3324/haematol.2024.286544. Online ahead of print. ABSTRACT Hematopoietic stem cell transplantation is a well-established treatment option for acquired aplastic anemia. Historically, …

Left Heart Abnormalities in Patients With Lung Disease, OSA, and Chronic Thromboemboli at Risk for or With Known Pulmonary Hypertension

Circ Heart Fail. 2025 May 29:e012912. doi: 10.1161/CIRCHEARTFAILURE.125.012912. Online ahead of print. ABSTRACT BACKGROUND: Patients with lung disease, sleep apnea, and chronic thromboemboli can develop …

Exploring lumen-apposing metal stents as a novel approach for managing walled-off necrosis in pediatric acute pancreatitis in Indian cohort: a prospective study

Clin Endosc. 2025 May 29. doi: 10.5946/ce.2024.315. Online ahead of print. ABSTRACT BACKGROUND/AIMS: Walled-off necrosis (WON) is a severe complication of acute pancreatitis in children, …

Pediatric Patient Experiences Using Medical Cannabis in Cancer Symptom Management as Reported by Parents of Children and Adolescents and by Young Adults

J Pediatr Hematol Oncol Nurs. 2025 May 29:27527530251318606. doi: 10.1177/27527530251318606. Online ahead of print. ABSTRACT Children, adolescents, and young adults (YAs) with cancer are using …