Paediatrics
Paediatrics

Age-Adjusted Dosing of Fludarabine for Lymphodepletion in CAR T-cell Therapy: A Clinical Trial Simulation Study

Blood Adv. 2025 Jul 3:bloodadvances.2025015928. doi: 10.1182/bloodadvances.2025015928. Online ahead of print. ABSTRACT Fludarabine (FLU) is used for lymphodepletion and improves the persistence and expansion of …

Association of Sleep Study Outcomes and Healthcare Utilization in Children with Sickle Cell Disease, a Multicenter Study

Blood Adv. 2025 Jul 3:bloodadvances.2025016312. doi: 10.1182/bloodadvances.2025016312. Online ahead of print. ABSTRACT Sickle cell disease (SCD) is associated with increased healthcare utilization. Sleep disorders have …