Paediatrics
Paediatrics

Consumer and community involvement in paediatric intensive care research across Australia and New Zealand: a protocol for a mixed-methods environmental scan

Res Involv Engagem. 2025 Jul 15;11(1):82. doi: 10.1186/s40900-025-00734-y. ABSTRACT BACKGROUND: Paediatric intensive care provides specialist expertise and support for critically ill children, often with complex …

Utility of patient-reported outcomes for pulmonary symptoms and sleep disturbance and impairment in children with systemic juvenile idiopathic arthritis

Pediatr Rheumatol Online J. 2025 Jul 15;23(1):74. doi: 10.1186/s12969-025-01126-y. ABSTRACT BACKGROUND: Patient-reported outcomes (PROs) are critical assessment tools for clinical practice, observational studies, and interventional …

Identifying the characteristics of and developing a predictive model for differentiating cancer-related musculoskeletal symptoms from juvenile idiopathic arthritis

Pediatr Rheumatol Online J. 2025 Jul 15;23(1):73. doi: 10.1186/s12969-025-01121-3. ABSTRACT BACKGROUND: Musculoskeletal (MSK) symptoms are a frequent presentation in pediatric patients and may arise from …

Development and validation of scales measuring self-efficacy and behavioral capability in managing common medical emergencies in dental clinics

BMC Med Educ. 2025 Jul 15;25(1):1059. doi: 10.1186/s12909-025-07663-0. ABSTRACT OBJECTIVES: Managing medical emergencies is a critical skill for dental professionals, yet many dental practitioners and …

Long-term efficacy and safety of arimoclomol in Niemann-Pick disease type C: Final results of the phase 2/3 NPC-002 48-month open-label extension trial

Mol Genet Metab. 2025 Jul 7;145(4):109189. doi: 10.1016/j.ymgme.2025.109189. Online ahead of print. ABSTRACT BACKGROUND: This paper presents efficacy and safety outcomes from the 48-month open-label …