Disease-modifying therapies for spinal muscular atrophy: Family experience, ethical considerations, and the role of social determinants of health
J Neuromuscul Dis. 2025 Sep 3:22143602251375561. doi: 10.1177/22143602251375561. Online ahead of print. ABSTRACT OBJECTIVES: Spinal muscular atrophy is a progressive neuromuscular condition associated with a …