Gene-edited CAR T cells: going the distance in B-ALL
Blood Adv. 2025 Sep 23;9(18):4755-4756. doi: 10.1182/bloodadvances.2025017508. NO ABSTRACT PMID:40986309 | DOI:10.1182/bloodadvances.2025017508
Paediatrics
Biomarkers of immune dysregulation and posttreatment inflammation in spinal muscular atrophy
Proc Natl Acad Sci U S A. 2025 Sep 30;122(39):e2506976122. doi: 10.1073/pnas.2506976122. Epub 2025 Sep 23. ABSTRACT Spinal Muscular Atrophy (SMA) is a neurodegenerative disorder …
Availability and affordability of cannabinoids for epilepsy treatment across different geographic settings-A survey from the ILAE Plant-Based Therapy Task Force
Epilepsia. 2025 Sep 23. doi: 10.1111/epi.18622. Online ahead of print. NO ABSTRACT PMID:40986286 | DOI:10.1111/epi.18622
Weighing the evidence: apixaban for pediatric leukemia
Blood Adv. 2025 Sep 23;9(18):4748-4749. doi: 10.1182/bloodadvances.2025016948. NO ABSTRACT PMID:40986308 | DOI:10.1182/bloodadvances.2025016948
Beyond the Clinic Walls: Hospitalists’ Role in Addressing Intimate Partner Violence and Social Drivers of Health
J Gen Intern Med. 2025 Sep 23. doi: 10.1007/s11606-025-09853-4. Online ahead of print. NO ABSTRACT PMID:40986217 | DOI:10.1007/s11606-025-09853-4
Descriptive characterization of ambulatory health states in Duchenne muscular dystrophy: Motor function trajectories and times to loss of ambulation
J Neuromuscul Dis. 2025 Sep 23:22143602251364694. doi: 10.1177/22143602251364694. Online ahead of print. ABSTRACT We described ambulatory Duchenne muscular dystrophy (DMD) progression, across multiple functional measures, …
Clinical and Laboratory Findings of Scrub Typhus in Children
Indian J Pediatr. 2025 Sep 23. doi: 10.1007/s12098-025-05763-9. Online ahead of print. NO ABSTRACT PMID:40986181 | DOI:10.1007/s12098-025-05763-9
Impact of SNP Variants in PON-1 or UGT1A1 on Iron Chelation Therapy Outcomes and Zinc Status in Thalassemia Major Patients
Biol Trace Elem Res. 2025 Sep 23. doi: 10.1007/s12011-025-04823-7. Online ahead of print. ABSTRACT Factors affecting iron chelation therapy outcomes are complex and should be …
Single-Cell Transcriptomics Reveals ITGA2-Mediated Metabolic Reprogramming and Immune Crosstalk in Pediatric Thyroid Carcinogenesis
Adv Sci (Weinh). 2025 Sep 23:e04088. doi: 10.1002/advs.202504088. Online ahead of print. ABSTRACT Pediatric papillary thyroid carcinoma (PPTC) has exhibited a progressive increase in incidence …
Characteristics of Cerebral Palsy in the Midwestern US
Ann Clin Transl Neurol. 2025 Sep 23. doi: 10.1002/acn3.70182. Online ahead of print. ABSTRACT OBJECTIVE: Cerebral palsy (CP) is the most common lifelong motor disability …