Neonatal Medicine
Neonatal Medicine

Respiratory outcomes of onasemnogene abeparvovec treatment for spinal muscular atrophy: national real-world cohort study

Eur J Pediatr. 2024 Dec 3;184(1):58. doi: 10.1007/s00431-024-05886-9. ABSTRACT Onasemnogene abeparvovec (OA) is a novel gene replacement therapy for patients with spinal muscular atrophy (SMA). …

Immunophenotyping and Activation Status of Maternal Lymphocytes to Predict Spontaneous Preterm Birth in Women With Threatened Preterm Labor: A Prospective Observational Study

Am J Reprod Immunol. 2024 Dec;92(6):e70015. doi: 10.1111/aji.70015. ABSTRACT PROBLEM: Preterm birth (PTB) remains the leading cause of neonatal morbidity and mortality. Identifying women at …

Clinical characteristics, treatment, and outcomes of provoked acute cerebral sinovenous thrombosis in patients <21 years old: findings from the Kids-DOTT Multinational Trial

Res Pract Thromb Haemost. 2024 Oct 23;8(7):102605. doi: 10.1016/j.rpth.2024.102605. eCollection 2024 Oct. ABSTRACT BACKGROUND: Prospective multicenter data on the treatment and outcomes of children with …