Comprehensive analysis of off-target and on-target effects resulting from liver-directed CRISPR-Cas9-mediated gene targeting with AAV vectors
Mol Ther Methods Clin Dev. 2024 Nov 4;32(4):101365. doi: 10.1016/j.omtm.2024.101365. eCollection 2024 Dec 12. ABSTRACT Comprehensive genome-wide studies are needed to assess the consequences of …