Dramatic response to Evinacumab in a North Indian girl with homozygous familial hypercholesterolemia
J Pediatr Endocrinol Metab. 2025 Jan 1;38(3):305-309. doi: 10.1515/jpem-2024-0506. Print 2025 Mar 26. ABSTRACT OBJECTIVES: Homozygous familial hypercholesterolemia (HoFH) is a rare inherited disorder of …