Pilocytic Astrocytoma in a Child with Spinal Muscular Atrophy Treated with Onasemnogene Abeparvovec
Mol Ther. 2025 Feb 15:S1525-0016(25)00115-7. doi: 10.1016/j.ymthe.2025.02.025. Online ahead of print. ABSTRACT Spinal muscular atrophy (SMA) is a severe neuromuscular disease, leading to progressive muscle …