A plain language summary of the SAPPHIRE clinical trial of apitegromab in children and young adults with spinal muscular atrophy
Paediatrics
A plain language summary of the SAPPHIRE clinical trial of apitegromab in children and young adults with spinal muscular atrophy
Paediatrics

A plain language summary of the SAPPHIRE clinical trial of apitegromab in children and young adults with spinal muscular atrophy

Expert Rev Neurother. 2025 Nov 13:1-20. doi: 10.1080/14737175.2025.2579903. Online ahead of print.

NO ABSTRACT

PMID:41233939 | DOI:10.1080/14737175.2025.2579903