Chest-sited intraventricular access devices for cerliponase alfa infusion in Batten disease at a single tertiary United Kingdom pediatric center
J Neurosurg Pediatr. 2025 Oct 31:1-8. doi: 10.3171/2025.7.PEDS25222. Online ahead of print. ABSTRACT OBJECTIVE: Cerliponase alfa is an enzyme replacement treatment for neuronal ceroid lipofuscinosis …