Month: <span>October 2025</span>
Month: October 2025

Chest-sited intraventricular access devices for cerliponase alfa infusion in Batten disease at a single tertiary United Kingdom pediatric center

J Neurosurg Pediatr. 2025 Oct 31:1-8. doi: 10.3171/2025.7.PEDS25222. Online ahead of print. ABSTRACT OBJECTIVE: Cerliponase alfa is an enzyme replacement treatment for neuronal ceroid lipofuscinosis …

Efficacy of a Ready-to-Feed Starter Liquid Infant Formula Containing 2-Fucosyllactose and Lacto-N-Neotetraose in Chinese Infants: Protocol for a Double Blind, Randomized Controlled Trial

JMIR Res Protoc. 2025 Oct 31;14:e66489. doi: 10.2196/66489. ABSTRACT BACKGROUND: Bioactive compounds, such as human milk oligosaccharides (HMOs), impact the development of the intestinal microbiome …

Risk and response adapted treatment in pediatric Epstein-Barr virus associated hemophagocytic lymphohistiocytosis

J Infect Dis. 2025 Oct 31:jiaf556. doi: 10.1093/infdis/jiaf556. Online ahead of print. ABSTRACT BACKGROUND: Hemophagocytic lymphohistiocytosis (HLH) is a rapidly progressive and often fatal disorder …

Treatment with Minicircle DNA Expressing a FGF23 Fragment in a Clinically relevant Mouse Model of X-Linked Hypophosphatemic Rickets

Adv Sci (Weinh). 2025 Oct 31:e08870. doi: 10.1002/advs.202508870. Online ahead of print. ABSTRACT X-linked hypophosphatemic rickets (XLHR) is a rare X-linked dominant skeletal dysplasia caused …