Discovery of Functionalized 1H-Benzo[d]imidazoles That Confer Protective Effects in a Phenotypic CLN3 Disease Patient-Derived iPSC Model
J Med Chem. 2025 Sep 1. doi: 10.1021/acs.jmedchem.5c01369. Online ahead of print. ABSTRACT The neuronal ceroid lipofuscinoses (NCLs) are rare and fatal autosomal pediatric neurodegenerative …